Fierce Pharma
Fierce Biotech
Fierce Healthcare
Fierce Life Sciences Events
Advertise
About Us
Biotech
Cell & Gene Therapy
Clinical Data
Venture Capital
Deals
Research
Medtech
Devices
Diagnostics
AI and Machine Learning
CRO
Special Reports
Trending Topics
Diabetes
Clinical Development
Biologics
Fierce 50
Special Report
Awards Gala
Resources
Fierce Events
Industry Events
Webinars
Podcasts
Whitepapers
Survey
Events
Subscribe
Trending T
Biotech
Cell & Gene Therapy
Clinical Data
Venture Capital
Deals
Research
Medtech
Devices
Diagnostics
AI and Machine Learning
CRO
Special Reports
Trending Topics
Diabetes
Clinical Development
Biologics
Fierce 50
Special Report
Awards Gala
Resources
Fierce Events
Industry Events
Webinars
Podcasts
Whitepapers
Survey
Events
Subscribe
Fierce Pharma
Fierce Biotech
Fierce Healthcare
Fierce Life Sciences Events
Advertise
About Us
genetic diseases
Biotech
'Clinical intuition' led FDA advisors to back Zevra's rare disease med
Zevra’s rare disease drug seems to be on the path to approval after gaining the backing of an FDA advisory committee, although the experts were split.
Annalee Armstrong
Aug 5, 2024 10:35am
Ultragenyx, Mereo's brittle bone drug sustains fracture rate cut
Jun 12, 2024 8:55am
Avidity therapy shows possible benefit in muscular dystrophy
Jun 12, 2024 7:00am
Otsuka pays Ionis $65M for European rights to rare disease drug
Dec 19, 2023 10:18am
Reneo pulls plug on rare disease asset, sinking stock 87%
Dec 14, 2023 10:16am
FDA launches new genetic metabolic disease advisory committee
Dec 12, 2023 12:35pm