Duchenne muscular dystrophy

DNA gene therapy gene editing helix CRISPR

Regenxbio starts pivotal study for DMD gene therapy

Regenxbio’s gene therapy improved muscle function for patients with DMD in a phase 1/2 study, with the biotech rolling the trial into a pivotal study.

Gabrielle Masson Nov 18, 2024 2:24pm

DMD gene therapy uses cells to stitch together mRNA in mice

Nov 14, 2024 3:10pm

Capricor shares more data for DMD therapy after initiating BLA

Oct 11, 2024 11:50am

Duchenne muscular dystrophy genetic test DMD

Young participant in Pfizer's DMD gene therapy trial dies

May 7, 2024 4:29pm

Sarepta's next DMD drug seems to get the job done in phase 2

Jan 29, 2024 10:49am

Pfizer’s DMD gene therapy now ‘main game in town,' CSO says

Oct 31, 2023 2:28pm